Base-edited Cynomolgus Monkeys mimic core symptoms of STXBP1 encephalopathy.

2022 Zongyang Lu, Siting He, Jian Jiang, Ling Zhuang, Yan Wang, Guang Yang, Xiaoyu Jiang, Yanhong Nie, Jiqiang Fu, Xiaotong Zhang, Yong Lu, Xinyan Bian, Hung-Chun Chang, Zhiqi Xiong, Xingxu Huang*, Zhen Liu*, Sun, Q.*