Lentiviral delivery of co-packaged?Cas9?mRNA and a?Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice.

2021 Ling, S., Yang, S., Hu, X., Yin, D., Dai, Y., Qian, X., Wang, D., Pan, X., Hong, J., Sun, X., Yang, H., Paludan, S. & Cai Y. *